PTC Therapeutics is focused on the development of orally administered small molecule drugs and gene therapy which regulate gene expression by targeting post-transcriptional control mechanisms in orphan diseases. The lead asset, sepiapterin, targets adult and paediatric patients with phenylketonuria and is in Phase III development. PTC Therapeutics listed on NASDAQ in 2013.
CEO
Stuart W. Peltz
Therapeutics
New Jersey, USA
Registered in England No. 3941653 | VAT No. GB 765 3567 96
© 2017 Rosetta Capital Limited | Authorised and regulated by the Financial Conduct Authority
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